Gene Therapy
Study Findings from National Eye Institute Provide New Insights into Gene Therapy
Published in Gene Therapy Weekly, December 22nd, 2011
2011 DEC 22 -- According to the authors of recent research published in the journal Human Molecular Genetics, "Defects in the photoreceptor-specific gene aryl hydrocarbon receptor interacting protein-like 1 (Aipl1) are associated with Leber congenital amaurosis (LCA), a childhood blinding disease with early-onset retinal degeneration and vision loss. Furthermore, Aipl1 defects are characterized at the most severe end of the LCA spectrum."
"The rapid photoreceptor degeneration and vision loss observed in the LCA patient population are mimicked in a mouse model lacking AIPL1. Using this model, we evaluated if gene replacement therapy using recent...
Want to see the full article?
We're a pay-per-view site for premium content. If you'd like to purchase this article, it's only $3.00.
Welcome to NewsRx!
Learn more about a six-week, no-risk free trial of Gene Therapy Weekly
Source: Gene Therapy Weekly (2011-12-22)
More Articles from Gene Therapy Weekly
- Gene Therapy
Data from Washington University Advance Knowledge in Gene Therapy - Guanidines
Data on Guanidines Described by Researchers at McGill University - Small Interference RNAs (siRNAs)
Data on Small Interference RNAs (siRNAs) Reported by Researchers at Michigan State University - Gene Therapy
Findings from INSERM in Gene Therapy Reported - Epidermolysis Bullosa
New Data from Iuliu Hatieganu University of Medicine & Pharmacy Illuminate Research in Epidermolysis Bullosa - Gene Therapy
New Data from Salk Institute Illuminate Research in Gene Therapy - More from this issue of Gene Therapy Weekly
NewsRx is Social
Follow us on your favorite social network by clicking on a button below:
Top Medical Newsletters
Awards
Best Health/Healthcare Content, 2012
Best Health/Healthcare Content, 2011
Best e-Business Site, 2010
Best e-Business Site, 2009
Best e-Business Site, 2008
Best e-Business Site, 2007
Best e-Business Site, 2006
Best Healthcare Content, 2005
Best Overall Internet Site, 2005
Best Interactive Site, 2005
Facts & Stats
NewsRx also is available at LexisNexis, Gale, ProQuest, Factiva, Dialog, Thomson Reuters, NewsEdge, and Dow Jones.
- Google 2010 PageRank: #2 Among Top Health News and Media Publications
- Google 2010 PageRank: #2 Among Top Science Publications in Biology/Physiology
- Google 2010 PageRank: #2 Among Top News and Media for the Business of Pharmaceuticals
- Amazon's Alexa 2010 PageRank: #2 News and Media Site for the Pharmaceutical Industry
